Research Pipelines

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Current Research Study in Pipeline 

∆6-25 Mice Model Creation - See Details 

Donate Here: ∆6-25 Mice Model Creation Campaign

Targeted Start Date	January, 3rd 2025
Estimated Timeline of ∆6-25 Mice Model Creation	March, 31st 2025
Number of Patients Exons 6 & 7 Skipping May Benefit	180 Patients
∆6-25  Mice Model Cost (Campaign's Goal)	$25,000

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Next Research Study in Pipeline

∆7-44 Deletion lncRNA Study - See Details

Targeted Start Date	March , 01st 2025
Estimated Completion Date	March, 01st 2026
Number of Patients Benefitting	All In-Frame Deletions
∆6-25  Mice Model Cost (Campaign's Goal)	$86,000

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How We Prioritize Our Research Study Funding

Each patient or parent of patients participating in our organization represent a population of patients that share the same mutation.

We prioritize research studies based on the severity of the mutations in our pipeline. This means more severe mutations have smaller window of opportunity to find any sort of solutions compared to less severe.